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Tag: Rare Diseases

Pfizer to offer low-cost drugs to 45 low-income countries

Global Markets Pharma -
Pfizer Inc. May 25th launched 'An Accord for a Healthier World.' This groundbreaking initiative aims to provide all of...

Cases of monkeypox are being investigated in Europe, the United States, Canada, and Australia

Global Markets Pharma -
Cases of monkeypox are being investigated in several European countries as well as the US, Canada and Australia, according...

FDA lifts ban on LogicBio’s clinical trial on pediatric patients with methylmalonic acidemia

Drug Development Pharma -
LogicBio Therapeutics, Inc., a clinical-stage company advancing a diversified pipeline of genetic medicines addressing rare disorders from infancy through...

Novo Nordisk raises 2022 outlook after strong quarter, shares up

EAEU Market Pharma -
Novo Nordisk targets higher sales and operating profit for the year on the back of projected profit growth in...

FDA Approves alpelisib as first and only treatment for PROS, a spectrum of rare conditions

Regulatory Pharma -
Novartis on Wednesday announced that the U.S. Food and Drug Administration (FDA) granted accelerated approval to Vijoice® (alpelisib) for...

Sanofi’s rare disease drug gets world’s first approval in Japan

Global Markets Pharma -
The Japanese Ministry of Health, Labor, and Welfare (MHLW) has granted marketing authorization for Xenpozyme® (olipudase alfa) for the...

U.S. FDA approves drug to treat seizures associated with Lennox-Gastaut Syndrome, a rare form of childhood epilepsy

Global Markets Pharma -
UCB, a global biopharmaceutical company, on Monday announced that FINTEPLA (fenfluramine) oral solution CIV has been approved in the...

Marinus Pharmaceuticals has achieved FDA approval for its first and sole drug

Global Markets Pharma -
Marinus Pharmaceuticals, Inc., a pharmaceutical company dedicated to the development of innovative therapeutics to treat seizure disorders, announced that...

Emmes makes 4th acquisition in CRO focused on rare diseases

Global Markets Pharma -
Emmes, a global, full-service Clinical Research Organization (CRO) dedicated to supporting the advancement of public health and biopharmaceutical innovation,...

illumina launches multiple-gene test to spot rare treatable cancers

Manufacturing Pharma -
Illumina, Inc. today announced the launch of TruSight™ Oncology (TSO) Comprehensive (EU), a single test that assesses multiple tumor...

Ergomed launches Rare Disease Innovation Center

Drug Development Pharma -
ERGOMED plc a leading Clinical Research Organization focused on rare disease drug development today announced the establishment of its...

EMA – New medicine for rare type of eye cancer

Global Markets Pharma -
EMA has recommended granting a marketing authorisation in the European Union (EU) for Kimmtrak (tebentafusp), a monotherapy for the...

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Disclaimer All content on pharmprom.net is for informational purposes only and does not constitute medical advice. The materials are intended exclusively for industry professionals and are not addressed to the general public.

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